主办：上海医药工业研究院
　　　中国药学会
ISSN 1672-9188   CN 31-1939/R   SLYHAA
World Clinical Drug
Brief analysis of research and development in gene therapy for rare diseases
YU Yinghui , CHEN Guiliang
World Clinical Drug . 2023, (12): 1339 -1344 .  DOI: 10.13683/j.wph.2023.12.017